Search Results for: blog eteplirsen might help treat duchenne muscular dystrophy

A Mother’s Plea for Both her Sons to Live

A small study was done that indicated that a drug called Eteplirsen could help treat the symptoms of Duchenne Muscular Dystrophy. A mother has started a petition asking for the FDA to approve the drug. One of her sons was in the study and improved. Her other son was not in the study and cannot have access to the drug. Sarpeta is a company that makes a drug called Eteplirsen. It was designed to treat the symptoms of Duchenne Muscular Dystrophy. New drugs are not simply distributed to pharmacies and placed on the shelves of drug stores. There are a … Continue reading →

New Medicines, Transgenic Cows, and an Ice Cream Truck

This week, the Special Needs Blog had a wide range of topics appear. There’s a blog about hypoallergenic milk, a music program donation, a couple of new medications for specific special needs, and even a blog about a fantastic Halloween costume! This Week in Review blog will catch you up on whatever you missed. Transgenic Cow Makes Hypoallergenic Milk Scientists have created a genetically altered cow hat produces milk that is hypoallergenic (in some ways, but not in others). Could this mean that, someday, we will have this type of milk on store shelves for people who have allergies to … Continue reading →

Eteplirsen Might Help Treat Duchenne Muscular Dystrophy

An experimental drug called Eteplirsen might be helpful for boys who have Duchenne muscular dystrophy. A small study was done that seems to indicate that the drug helps slow the progression of the disease. The FDA would need to approve of Eteplirsen before the drug can be sold on the market. Muscular dystrophy is a disease that is characterized by progressive muscle weakness and wasting. There are nine different types. Duchenne muscular dystrophy is the most common form of the disease in children. According to the Mayo Clinic, Duchenne muscular dystrophy results from an absence of dystrophin, which is a … Continue reading →